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Modalis Therapeutics

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Epigenome editing from Japan

Modalis Therapeutics is a Japanese clinical-stage company developing epigenome editing therapies using its proprietary CRISPR-GNDM (Guide Nucleotide-Directed Modulation) platform. The company focuses on neurological disorders and has a collaboration with JCR Pharmaceuticals for CNS gene therapy.

Founded2016
HQTokyo, Japan
CEOKenichiro Arai
TickerTSE:4883
Total Funding$120M

Pipeline

Drug / ProgramIndicationPhaseTechnology
MDL-101Muscular DystrophyPreclinicalCRISPR-GNDM
JCR/Modalis CNS programCNS DisordersPreclinicalEpigenome Editing

Key People

Kenichiro AraiCEO

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