Biotech Company Profiles

Explore the leading gene editing and longevity companies shaping the future of medicine. Detailed profiles with pipeline data, funding, key people, and technologies.

34 companies

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CRISPR Therapeutics

Public

Pioneering CRISPR-based medicines

CRISPR-Cas9
NASDAQ:CRSP$2.8B2013
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Intellia Therapeutics

Public

In vivo CRISPR gene editing

CRISPR-Cas9LNP Delivery
NASDAQ:NTLA$2.1B2014
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Beam Therapeutics

Public

Precision base editing medicines

Base Editing (CBE/ABE)
NASDAQ:BEAM$1.5B2017
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Verve Therapeutics

Public

Gene editing for heart disease

Base EditingLNP Delivery
NASDAQ:VERV$900M2018
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Editas Medicine

Public

Editing genes to treat disease

CRISPR-Cas9CRISPR-Cas12a
NASDAQ:EDIT$1.2B2013
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Prime Medicine

Public

Search-and-replace gene editing

Prime Editing
NASDAQ:PRME$700M2019
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Caribou Biosciences

Public

Next-gen CRISPR for cell therapy

CRISPR-Cas9chRDNA
NASDAQ:CRBU$600M2011
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Altos Labs

Private

Restoring cell health to reverse disease

Epigenetic ReprogrammingYamanaka Factors
$3.0B2021
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Life Biosciences

Private

Reversing aging through partial epigenetic reprogramming — first in humans

Partial Epigenetic ReprogrammingYamanaka Factors (OSK)AAV Gene Therapy
$175M2017
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Retro Biosciences

Private

Adding 10 years to healthy human lifespan

Partial ReprogrammingAutophagy
$180M2021
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Chroma Medicine

Private

Epigenome editing — gene control without cutting

Epigenome Editing
$335M2020
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Wave Life Sciences

Public

Programmable RNA editing

RNA Editing (ADAR)
NASDAQ:WVE$1.0B2012
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Sangamo Therapeutics

Public

Zinc finger pioneers

Zinc Finger Nucleases (ZFN)Gene Therapy
NASDAQ:SGMO$1.5B1995
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Insilico Medicine

Private

AI-powered drug discovery for aging

AI Drug DiscoveryGenerative Biology
$400M2014
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NewLimit

Private

Epigenetic reprogramming for human rejuvenation

Epigenetic Reprogramming
$130M2021
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Turn Biotechnologies

Private

mRNA epigenetic reprogramming

mRNA Epigenetic Reprogramming
$60M2018
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Colossal Biosciences

Private

De-extinction and species preservation through gene editing

CRISPR-Cas9Synthetic BiologyComputational Genomics
$270M+2021
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Isomorphic Labs

Private

AI-first drug discovery from DeepMind

AI Drug DiscoveryAlphaFoldProtein Structure Prediction
$600M2021
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EdiGene / Correcta Therapeutics

Private

China's CRISPR and RNA editing leader

CRISPR-Cas9RNA Editing (LEAPER)
$300M2015
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HuidaGene Therapeutics

Private

Next-gen CRISPR for neurological diseases

CRISPR-Cas12iCRISPR-Cas13YhfCas12Max
$150M2018
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CorrectSequence Therapeutics

Private

Transformer base editing from China

Base Editing (tBE)
$80M2019
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Cellectis

Public

TALEN pioneers for off-the-shelf CAR-T

TALENGene Editing
NASDAQ:CLLS$800M1999
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BioNTech

Public

mRNA giant expanding into gene editing

mRNACRISPR-Cas9Cell Therapy
NASDAQ:BNTX$2.5B+2008
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Tune Therapeutics

Private

Tuning genes without cutting DNA

Epigenome Editing
$300M2020
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Modalis Therapeutics

Public

Epigenome editing from Japan

Epigenome Editing (CRISPR-GNDM)
TSE:4883$120M2016
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ToolGen

Public

Korea's CRISPR pioneer

CRISPR-Cas9ZFNTALEN
KOSDAQ:199800$150M1999
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bit.bio

Private

Coding biology to reprogram human cells

Cell Reprogramming (opti-ox)Gene Editing
$150M2016
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Cimeio Therapeutics

Private

Shielded cell therapy via gene editing

CRISPR-Cas9Shielded Cell Therapy
$150M2020
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Eyestem Research

Private

India's stem cell and gene therapy pioneer

iPSCGene EditingCell Therapy
$15M2015
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Juvenescence

Private

Multi-approach anti-aging therapeutics

Small MoleculesSenolyticsAI Drug Discovery
$250M2017
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MeiraGTx

Public

Precision AAV gene therapy for the eye, brain, and salivary glands

AAV Gene Therapy
NASDAQ:MGTX$400M+2015
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Benitec Biopharma

Public

Gene silencing with DNA-directed RNA interference (ddRNAi)

ddRNAi (DNA-directed RNA Interference)AAV Gene Therapy
ASX:BLT$100M+2002
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Cambrian Biopharma

Private

A portfolio approach to drug aging itself

SenolyticsEpigenetic ModulationProteostasisMetabolic Optimization
$160M+2017
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Prime Medicine

Public

Precision gene editing with prime editing technology

Prime Editing
NASDAQ:PRME$500M+2019
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