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Gene Therapy ROI Calculator

Investor Edition: Probability-weighted pipeline valuation for gene editing companies. Select a company to analyze risk-adjusted net present value (rNPV) based on phase success rates, market size, pricing assumptions, and time to market.

Discount Rate: 10%
5%20%
Scenario (adjusts market penetration)
Company

CRISPR Therapeutics

CRSP · Market Cap: $3.5B · Cash: $1.8B

4 programs

Total Pipeline rNPV

$16.9B

Risk-adjusted, base case

Current Market Cap

$3.5B

Approximate

rNPV / Market Cap

4.82x

Potentially undervalued

Risk-Adjusted NPV by Program

Casgevy (SCD)Approved$11.0B
Casgevy (TDT)Approved$5.3B
CTX110 (CAR-T)Phase 1/2$315.6M
CTX460 (AATD)Preclinical$282.2M

Pipeline Detail & Adjustments

Adjust market penetration and price per patient to model different assumptions.

ProgramPhasePatientsPenetrationPrice/PatientP(Success)YearsrNPV

Casgevy (SCD)

Sickle Cell Disease

Approved100,000
5.0%
$2.2M
100.0%Now$11.0B

Casgevy (TDT)

Transfusion-Dependent Thalassemia

Approved30,000
8.0%
$2.2M
100.0%Now$5.3B

CTX110 (CAR-T)

Non-Hodgkin Lymphoma

Phase 1/270,000
10.0%
$400K
15.0%3yr$315.6M

CTX460 (AATD)

Alpha-1 Antitrypsin Deficiency

Preclinical100,000
5.0%
$2.0M
5.0%6yr$282.2M
Total Pipeline rNPV$16.9B

Industry Phase Success Rates (BioMedTracker/Citeline)

Preclinical

5%

to approval

Phase 1

10%

to approval

Phase 1/2

15%

to approval

Phase 2

25%

to approval

Phase 2/3

45%

to approval

Phase 3

60%

to approval

Approved

100%

to approval

Methodology

Expected Revenue (per program)

Target Patients x Penetration x Price/Patient

Risk-Adjusted Revenue

Expected Revenue x P(Success for Phase)

Program rNPV

Risk-Adjusted Revenue / (1 + Discount Rate)^Years

Total Pipeline rNPV

Sum of all Program rNPVs

This is an educational tool for understanding biotech pipeline valuation concepts. It is NOT investment advice. Real valuations involve far more factors including competition, IP, management, manufacturing, and market dynamics. Past phase success rates do not guarantee future outcomes. Market caps and cash positions are approximate and may not reflect current values. Phase success rates are derived from BioMedTracker/Citeline industry data.